When faced with the myriad diseases and equally numerous targets for potential drugs the company could pursue, Kewalramani ...

Repositioning genes awakens fetal hemoglobin to treat disease. CRISPR editing may change future gene therapy. Researchers ...

Researchers have found a promising new method for gene therapy. They successfully restarted inactive genes by bringing them ...

Although sickle cell disease (SCD) is not as widespread in the Philippines compared to other populations, it is still worth ...

CRSP bets on Casgevy to drive growth, but its extremely high price tag and slow rollout test investor patience in a crowded ...

The double line on a pregnancy kit always brings joy and anticipation, but beyond the happiness, the mother’s health takes ...

EXTON, PA, June 04, 2025 (GLOBE NEWSWIRE) -- Despite the promise of new curative strategies for beta thalassemia, such as Casgevy (Vertex) and Zynteglo (bluebird bio), most transfusion-dependent ...