The patient, who is in his 30s, got the one-time intravenous infusion at the Infusion and Chemotherapy Treatment Center at ...

CRF acquired Spark Therapeutics, Inc.’s SPK-7001 CHM gene therapy assets and is analyzing long-term data to identify ...

Even when promising clinical trials exist, and the FDA allows expanded access, rare disease patients like my granddaughter ...

The trial is funded through Abu Dhabi’s Healthcare Research and Innovation Fund Clinical development activities will commence at Cleveland Clinic Abu Dhabi in 2026 MERTK-related retinitis pigmentosa ...

Despite innovative new research, many cell and gene therapies do not make it all the way to the patients. Researchers and ...

NEW YORK--(BUSINESS WIRE)-- Neurogene Inc. (Nasdaq: NGNE), a clinical-stage company founded to bring life-changing genetic medicines to patients and families affected by rare neurological diseases, ...

AUSTIN, Texas, Nov. 24, 2025 /PRNewswire/ -- Genprex, Inc. ("Genprex" or the "Company") (NASDAQ: GNPX), a clinical-stage gene therapy company focused on developing life-changing therapies for patients ...

The clinical trial participant who was hospitalized for severe complications after receiving the high dose of Neurogene’s experimental Rett syndrome gene therapy has died. Neurogene disclosed the ...

DUBLIN--(BUSINESS WIRE)--The "Cell and Gene Therapy CRO Market: Industry Trends and Global Forecasts, Till 2035 - Distribution by Type of Cell Therapy, Type of Genetic Modification, Stage of ...

Creative Biolabs is helping researchers overcome challenges of gene therapy research by providing analytical testing ...

Escandon is the founder and principal of DGBI Clinical Research and Ethics Consulting, a consultancy for the biotechnology industry. Caplan is Mitty professor of medical ethics at the NYU Grossman ...