A single base change can create a devastating genetic disorder or a beneficial ... often resulting in a frameshift One form of beta-thalassemia Deletion One or more nucleotides is "skipped ...

Known as Zynteglo in Europe where it is approved to treat the rare blood disorder beta-thalassemia, the gene therapy has been given the all-clear by bluebird’s scientists after reviewing the ...

While gene therapy has emerged as a promising alternative for treating beta-thalassemia, hematopoietic stem cell transplantation (HSCT) remains the only widely accessible curative option for this ...

Michelle Harlan, who has sickle beta thalassemia, wants to help others by getting a doctoral degree in clinical psychology.

The Rutgers Cancer Institute recently became a designated gene therapy treatment center for sickle cell anemia and beta-thalassemia, joining a small group of medical centers that currently provide ...

From STAT’s Andrew Joseph: AstraZeneca said this morning it was buying the Belgian cell therapy company EsoBiotec for $425 million upfront, building out another cancer-targeting approach.

Read on to know about some of the common genetic blood disorders. Half matched bone marrow transplant can be 100 per cent successful now for beta thalassemia patients, says a new research.